Current Edition

Potential Therapies in the R&D Pipeline for Facioscapulohumeral Muscular Dystrophy

Facioscapulohumeral MD, likely the most prevalent form of MD,
currently has no cure, but several factors point to the potential for
successful development of a disease-modifying FSHD treatment in
the near future. Raymond A. Huml, Lucie Undus, Meredith L. Huml,
and Margaret Dean discuss how the number of interventional trials
to treat FSHD is increasing sharply.