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Regional News

Roche’s aim to widen Evrysdi’s label nabs speedy FDA review in young spinal muscular atrophy patients

Now poised for a speedy trip through the FDA's regulatory review, Roche’s oral challenger in spinal muscular atrophy (SMA) could soon pick up a nod to cover all patie...
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Regional News

After its $7.6B buyout fell through, Sobi scores NICE backing for rare disease drug Aspaveli

After rare disease drugmaker Sobi reportedly had a buyout scuppered by pharma giant AstraZeneca, the company has picked up a win that stands to bolster its Aspaveli l...
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Europe

Researchers Develop Diagnostic for Rare Cancer-Generated Glycoproteins

Engineered chemical trap detects rare glycoproteins emitted as cancer first develops. Researchers at the Georgia Institute of Technology have designed a boronic acid ...
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